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  • Global companies expand business in expensive orphan drugs
  • by Lee, Tak-Sun | translator Byun Kyung A | Aug 20, 2020 06:24am
Pfizer's ATTR-CM treatment Vyndamax approved by the Korean health authority
Shares same substance with Vyndaqel approved in 2015, but has different indication
Healthcare reimbursement is an issue for the expensive drug with yearly expense at KRW 300 million
 ¡ã Vyndaql approved for the Korean market in 2015. Shares the same substance with Vyndmax but indicated for different disease.
As global pharmaceutical companies are on to expanding businesses in drugs for rare diseases, the companies are now winning item approvals in South Korean markets. Rare diseases have limited patient size and insufficient treatment options, but the drugs are expensive enough for the companies to seek for profit.

On Aug. 19, Ministry of Food and Drug Safety (MFDS) approved Pfizer Pharmaceutical Korea¡¯s Vyndamax 61 mg capsule (tafamidis). The medicine is indicated to treat cardiomyopathy of wild-type or hereditary transthyretin-mediated amyloidosis (ATTR-CM) in adults to reduce cardiovascular mortality and cardiovascular-related hospitalization. Although the patient size is small, the disease is known to develop a
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