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  • First drug for ultra rare Batten disease Brineura approved
  • by Lee, Tak-Sun | translator Byun Kyung A | Sep 11, 2020 06:28am
Healthcare consulting company Meditip processed approval for Korean market on the first Batten disease medication
The first treatment for a pediatric rare disease, Batten disease, has received the South Korean health authority¡¯s approval. As Batten disease is an inherited metabolic disorder that can cause loss of sight, the new treatment could give hopes to the patients and their families.

Ministry of Food and Drug Safety (MFDS) has approved Brineura 150 mg injection, supplied by MediTip, on Sept. 8. The product is indicated to treat ceroid lipofuscinosis type 2 (CLN2), also known as tripeptidyl peptidase 1 (TPP1) deficiency.

Recently, TPP1 or CLN2 is widely known as Batten disease. The disease is an inherited metabolic disorder, discovered by a Pediatric Doctor Batten in 1903. It is considered as an ultra rare disease with
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