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  • 6 cases of Ultomiris & 1 case of Spinraza were pre-approved
  • by Lee, Hye-Kyung | translator Choi HeeYoung | Dec 9, 2021 05:58am
The HIRA released a case of deliberation by the Medical Review and Assessment Committee last month
Benefits for pre-approval of six new PNH patients for Ultomiris administration were approved and four cases were rejected. There were no applications for new salary administration for Soliris, but two applications for pre-approval for new aHUS patients were not accepted.

In the case of Spinraza, a treatment for Spinal Muscular Atrophy (SMA), one application for new patient benefits and two data supplementations were decided. Of the 25 monitoring reports, 23 were approved and 2 were disapproved.
The HIRA conducted deliberation on six items, including Soliris and Ultomiris, and whether hospitalization fees were recognized. According to the results of the deliberation on the 2nd, Soliris decided to approve 33 PNH
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