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  • Vonjo receives orphan drug designation in Korea
  • by Eo, Yun-Ho | translator Kang, Shin-Kook | Sep 6, 2024 05:48am
Another treatment for myelofibrosis
MFDS announces its use for patients with platelet (blood clotting cells) levels below 50¡¿10⁹/L
Demonstrated 35% or greater spleen volume reduction from baseline through Phase III PERSIST-2 trial

The oral myelofibrosis drug Vonjo has been designated as an orphan drug in Korea.

The Ministry of Food and Drug Safety announced so on the 3rd through an orphan drug designation.

Specifically, the drug is indicated for ¡®adults with intermediate or high-risk primary or secondary (post-polycythemia vera or post-essential thrombocythemia) myelofibrosis (MF) with a platelet count
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