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  • New drug 'Wainua' for amyloid polyneuropathy receives ODD
  • by Eo, Yun-Ho | translator Hong, Ji Yeon | Mar 7, 2025 05:55am
Gained attention as the only treatment option with once-monthly administration
Demonstrated a reduction in transthyretin concentration through the Phase 3 trial
 ¡ã Product photo of Wainua
A new drug, 'Wainua,' for the treatment of amyloid polyneuropathy has been designated as an orphan drug in South Korea.

On March 5, the Ministry of Food and Drug Safety (MFDS) notified of the orphan drug

The drug is indicated for the treatment of hereditary transthyretin-mediated amyloidosis (ATTRv-PN).

Wainua (eplontersen) is a treatment for ATTRv-PN administered through subcutaneous injection once every month at home. This drug has been designed to target protein-producing liver using a new LICA technology.

ATTRv-PN is a progressive disease where abnormal protein deposits build up in the body's organs and tissues. It is a deteriorative disease that causes neuropathy in peripheral nerves. If the diseas
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