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  • Novartis, PNH drug 'Fabhalta' enters drug pricing nego.
  • by Eo, Yun-Ho | translator Hong, Ji Yeon | Apr 10, 2025 05:56am
The NHIS process began after passing the Drug Reimbursement Evaluation Committee (DREC) in March
It is expected to overcome limitations related to conventional C5 inhibiotrs
 ¡ã Product photo of Fabhalta
The new oral drug 'Fabhalta' has entered the last phase of receiving approval for insurance reimbursement.

According to industry sources, Novartis Korea¡¯s ¡¯Fabhalta (iptacopan),¡¯ a treatment for paroxysmal nocturnal hemoglobinuria (PNH), is under negotiations for drug pricing.

Consequently, attention is gaining to whether another treatment option for PNH would emerge.

PNH is a rare disease estimated to occur in approximately 1.5 individuals per 1 million globally.

Until now, the treatment for PNH has relied on C5 inhibitors. In 2010, ¡¯Soliris (eculizumab)¡¯ was first approved in South Korea, and 'Ultomiris (ravulizumab)' has been used for PNH treatment since its approval in 2022. Both treatment option
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