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  • ¡®Oral drug Fabhalta changes PNH treatment paradigm'
  • by Son, Hyung Min | translator Alice Kang | Apr 29, 2025 05:56am
Youngil Koh, Professor of Hematology/Medical Oncology, Seoul National University Hospital
Overcomes the limitations of existing C5 inhibitors... Improving anemia and blood transfusion dependence
First oral drug to enter the market... ¡±Expected to improve treatment satisfaction¡±
 ¡ã Youngil Koh, Professor of Hematology/Medical Oncology, Seoul National University Hospital
¡°While significant progress has been made in the treatment of paroxysmal nocturnal hemoglobinuria (PNH), unmet needs remain. Given the relatively young age of patients, there is an increasing emphasis on the need for treatment strategies that not only ensure survival but also improve anemia and enable patients to return to their daily lives. Therefore, I believe that Fabhalta, which improves ease of administration and has been shown to be effective in improving anemia, will become more widely used."

Youngil Koh, Professor of Hematology/Medical Oncology, at Seoul National University Hospital, emphasized so in a recent interview with Dailypharm regarding the paradigm shift being made in the PNH treatment landscape.
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