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  • 'Vonjo' for myelofibrosis expected to be marketed in KOR
  • by Eo, Yun-Ho | translator Hong, Ji Yeon | Jun 5, 2025 06:11am
A competitor to 'Jakabi'
The Ministry of Food and Drug Safety (MFDS) is conducting approval review¡¦'Vonjo' is expected to obtain official approval this year
Demonstrated a spleen volume reduction by 35% through the Phase 3 PERSIST-2 study
 ¡ã Product photo of Vonjo
The oral myelofibrosis treatment 'Vonjo' is expected to be commercialized in Korea.

According to industry sources, the Ministry of Food and Drug Safety is conducting an approval review of Vonjo (pacritinib). This drug obtained orphan drug designation (ODD) in September of last year.

Vonjo is indicated for 'treatment of intermediate-risk or high-risk adult patients with myelofibrosis who have plate count below 50¡¿10⁹/L.'

Vonjo is regarded as a competitor of Novartis' 'Jakabi (ruxolitinib)' and it obtained accelerated approval from the U.S. Food and Drug Administration (FDA) in 2022. It is a novel oral kinase inhibitor that does not inhibit Janus kinase 1 (JAK1 )but instead inhibits JAK2 and IRAK1.

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