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  • Luxturna shows signif improvement in 3 out of 6 patients
  • by Lee, Tak-Sun | translator Hong, Ji Yeon | Sep 3, 2025 06:09am
high-price drug that costs approximately KRW 300 million
HIRA disclosed the latest performance evaluation results¡¦half of the patients were successful
Luxturna (voretigene neparvovec, Novartis), a one-shot gene therapy that costs approximately KRW 300 million, showed clinically significant changes set by reimbursement criteria in only half of the patients.

As indicated in the performance evaluation results disclosed last year, the effectiveness was only 50%.

The Health Insurance Review & Assessment Service (HIRA) disclosed the latest performance evaluation results for Luxturna on August 29.

Luxturna is a gene therapy for patients with inherited retinal disease, administered as a single subretinal injection in each eye.

The ceiling price for one vial is KRW 325.8 million, with a patient co-payment of approximately KRW 10.5 million per person.

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