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  • Ipsen's Bylvay is officially launched in Korea
  • by Son, Hyung Min | translator Alice Kang | Oct 20, 2025 06:06am
New Milestone in PFIC Treatment
Will serve as a new turning point in treating PFIC
First oral therapy for an ultra-rare liver disease, reimbursed from October 2025
Marks a major milestone in access for pediatric patients with limited treatment options...¡°Provides an alternative to liver transplantation¡¦expected to improve quality of life for pediatric patients¡±
 ¡ã From the left: Professor Ji-hyu Seo (Gyeongsang National University Hospital), Professor Seok-hee (Asan Medical Center), and Professor Hong Ioh (Severance Hospital)
 Ipsen Korea is introducing a treatment for progressive familial intrahepatic cholestasis (PFIC), an extremely rare hereditary liver disease, to the domestic market. This launch opens new hope for pediatric patients who previously had no treatment option beyond liver transplantation.

Bylvay has been selected as the first product under Korea¡¯s ¡°Simultaneous Review & Negotiation Pilot Program,¡± which streamlines approval and reimbursement procedures. The drug has been covered by national health insurance since October 2025, representing a symbolic step forward in improving access to rare-disease therapies.

On October 18, Ipsen Korea held a press conference at Sofitel Seoul Lotte World to commemorate the p
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